Found 8 results
Author Title [ Type(Desc)] Year
Filters: Keyword is RNA Splicing  [Clear All Filters]
Journal Article
H. Yin, Moulton, H. M., Betts, C., and Wood, M., CPP-directed oligonucleotide exon skipping in animal models of Duchenne muscular dystrophy., Methods in molecular biology (Clifton, N.J.), vol. 683, pp. 321-38, 2011.
H. Yin, Moulton, H. M., Betts, C., and Wood, M., CPP-directed oligonucleotide exon skipping in animal models of Duchenne muscular dystrophy., Methods Mol Biol, vol. 683, pp. 321-38, 2011.
M. Nizzardo, Simone, C., Salani, S., Ruepp, M. - D., Rizzo, F., Ruggieri, M., Zanetta, C., Brajkovic, S., Moulton, H. M., Müehlemann, O., Bresolin, N., Comi, G. P., and Corti, S., Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy Δ7 mouse model phenotype., Clin Ther, vol. 36, no. 3, pp. 340-56.e5, 2014.
Y. Dang, van Heusden, C., Nickerson, V., Chung, F., Wang, Y., Quinney, N. L., Gentzsch, M., Randell, S. H., Moulton, H. M., Kole, R., Ni, A., Juliano, R. L., and Kreda, S. M., Enhanced delivery of peptide-morpholino oligonucleotides with a small molecule to correct splicing defects in the lung., Nucleic Acids Res, vol. 49, no. 11, pp. 6100-6113, 2021.
G. McClorey, Fall, A. M., Moulton, H. M., Iversen, P. L., Rasko, J. E., Ryan, M., Fletcher, S., and Wilton, S. D., Induced dystrophin exon skipping in human muscle explants., Neuromuscular disorders : NMD, vol. 16, no. 9-10, pp. 583-90, 2006.
H. M. Moulton and Moulton, J. D., Morpholinos and their peptide conjugates: therapeutic promise and challenge for Duchenne muscular dystrophy., Biochim Biophys Acta, vol. 1798, no. 12, pp. 2296-303, 2010.
H. M. Moulton and Moulton, J. D., Morpholinos and their peptide conjugates: therapeutic promise and challenge for Duchenne muscular dystrophy., Biochimica et biophysica acta, vol. 1798, no. 12, pp. 2296-303, 2010.
S. Abes, Moulton, H. M., Clair, P., Prevot, P., Youngblood, D. S., Wu, R. P., Iversen, P. L., and Lebleu, B., Vectorization of morpholino oligomers by the (R-Ahx-R)4 peptide allows efficient splicing correction in the absence of endosomolytic agents., Journal of controlled release : official journal of the Controlled Release Society, vol. 116, no. 3, pp. 304-13, 2006.