Found 16 results
Author [ Title(Desc)] Type Year
Filters: Keyword is Morpholinos  [Clear All Filters]
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M. Nizzardo, Simone, C., Salani, S., Ruepp, M. - D., Rizzo, F., Ruggieri, M., Zanetta, C., Brajkovic, S., Moulton, H. M., Müehlemann, O., Bresolin, N., Comi, G. P., and Corti, S., Effect of combined systemic and local morpholino treatment on the spinal muscular atrophy Δ7 mouse model phenotype., Clin Ther, vol. 36, no. 3, pp. 340-56.e5, 2014.
X. Gao, Zhao, J., Han, G., Zhang, Y., Dong, X., Cao, L., Wang, Q., Moulton, H. M., and Yin, H., Effective dystrophin restoration by a novel muscle-homing peptide-morpholino conjugate in dystrophin-deficient mdx mice., Mol Ther, vol. 22, no. 7, pp. 1333-1341, 2014.
Y. Echigoya, Nakamura, A., Nagata, T., Urasawa, N., Lim, K. Rowel Q., Trieu, N., Panesar, D., Kuraoka, M., Moulton, H. M., Saito, T., Aoki, Y., Iversen, P., Sazani, P., Kole, R., Maruyama, R., Partridge, T., Takeda, S. 'ichi, and Yokota, T., Effects of systemic multiexon skipping with peptide-conjugated morpholinos in the heart of a dog model of Duchenne muscular dystrophy., Proc Natl Acad Sci U S A, vol. 114, no. 16, pp. 4213-4218, 2017.
Y. Dang, van Heusden, C., Nickerson, V., Chung, F., Wang, Y., Quinney, N. L., Gentzsch, M., Randell, S. H., Moulton, H. M., Kole, R., Ni, A., Juliano, R. L., and Kreda, S. M., Enhanced delivery of peptide-morpholino oligonucleotides with a small molecule to correct splicing defects in the lung., Nucleic Acids Res, vol. 49, no. 11, pp. 6100-6113, 2021.
B. Wu, Cloer, C., Lu, P., Milazi, S., Shaban, M., Shah, S. N., Marston-Poe, L., Moulton, H. M., and Lu, Q. L., Exon skipping restores dystrophin expression, but fails to prevent disease progression in later stage dystrophic dko mice., Gene Ther, vol. 21, no. 9, pp. 785-93, 2014.